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#apaperaday: Nonclinical data supporting orphan medicinal product designations: lessons from rare neurological conditions

An older paper (2017) by Sheean et al from Drug Discovery Today on proper use of animal model data for orphan drug designation.

Investigating the Potential for Sulforaphane to Attenuate Gastrointestinal Dysfunction in mdx Dystrophic Mice

#apaperaday: Investigating the Potential for Sulforaphane to Attenuate Gastrointestinal Dysfunction in mdx Dystrophic Mice

Today’s paper by Swiderski et al on testing if sulforaphane (SFN) can improve skeletal muscle and gastric muscle function in mdx mice.

#apaperaday: Pharmacological Profile of Viltolarsen for the Treatment of Duchenne Muscular Dystrophy: A Japanese Experience

Today’s a paper a day pick is from clinical pharmacology: advances and applications on viltolarsen by Roshmi and Prof. Toshi Yokota.

#apaperaday: Dystrophin deficiency affects human astrocyte properties and response to damage

Today’s pick is by Lange et al from Glia. It is a study on astrocyte properties in cells with and without dystrophin.

#apaperaday: Alteration of skeletal and cardiac muscles function in DBA/2J mdx mice background: a focus on high intensity interval training

Baati et al in Intractable and Rare Disease Research on the impact of high intensity training in d2/mdx mice.

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