Projects

EURO-NMD, ERN for Rare Neuromuscular Diseases, spans 14 European countries, with 61 reference centres that oversee more than 100,000 patients.…

The World Duchenne Organization and several of its members have been advocating for better use of Duchenne data, which is…

First project of this scale to improve characterisation of brain involvement in Duchenne and Becker Muscular Dystrophy

VISION-DMD is a collaborative global project aiming to develop a safe, effective and affordable therapy for Duchenne Muscular Dystrophy (DMD).…

A rare disease affects less than 5 in 10.000 persons, and the 50% of them are children. Keeping this number…

The [email protected] consortium is exploring the opportunities of moving clinical trials from the traditional clinic setting to the participant's immediate…