From diagnosis to therapy in Duchenne muscular dystrophy
Babbs A, Chatzopoulou M, Edwards B, et al. From diagnosis to therapy in Duchenne muscular dystrophy. Biochem Soc Trans 2020…
New Developments in Diagnosis, Treatment, and Management of Duchenne Muscular Dystrophy
Gieron-Korthals M, Fernandez R. New Developments in Diagnosis, Treatment, and Management of Duchenne Muscular Dystrophy. Adv Pediatr 2020;67:183-196 Key…
Comprehensive genetic analysis of 961 unrelated Duchenne Muscular Dystrophy patients: Focus on diagnosis, prevention and therapeutic possibilities
Kumar SH, Athimoolam K, Suraj M, et al. Comprehensive genetic analysis of 961 unrelated Duchenne Muscular Dystrophy patients: Focus on…
Update on Muscular Dystrophies with Focus on Novel Treatments and Biomarkers
Datta N, Ghosh PS. Update on Muscular Dystrophies with Focus on Novel Treatments and Biomarkers. Curr Neurol Neurosci Rep 2020;20:14…
Targeted Treatments for Inherited Neuromuscular Diseases of Childhood
Fay AJ, Knox R, Neil EE, Strober J. Targeted Treatments for Inherited Neuromuscular Diseases of Childhood. Semin Neurol 2020;40:335-341 …
Common therapeutic advances for Duchenne muscular dystrophy (DMD)
Salmaninejad A, Jafari Abarghan Y, Bozorg Qomi S, et al. Common therapeutic advances for Duchenne muscular dystrophy (DMD). Int J…
Characterizing Enrollment in Observational Studies of Duchenne Muscular Dystrophy by Race and Ethnicity
Barnard AM, Riehl SL, Willcocks RJ, Walter GA, Angell AM, Vandenborne K. Characterizing Enrollment in Observational Studies of Duchenne Muscular…
New and emerging pharmacotherapy for duchenne muscular dystrophy: a focus on synthetic therapeutics
Grages SM, Bell M, Berlau DJ. New and emerging pharmacotherapy for duchenne muscular dystrophy: a focus on synthetic therapeutics. Expert…
The evolution of patient-focused drug development and Duchenne muscular dystrophy
Crossnohere NL, Fischer R, Crossley E, Vroom E, Bridges JF. The evolution of patient-focused drug development and Duchenne muscular dystrophy.…
Current and emerging therapies in Becker muscular dystrophy (BMD)
Angelini C, Marozzo R, Pegoraro V. Current and emerging therapies in Becker muscular dystrophy (BMD). Acta myologica : myopathies and…
