New Developments in Diagnosis, Treatment, and Management of Duchenne Muscular Dystrophy

Gieron-Korthals M, Fernandez R. New Developments in Diagnosis, Treatment, and Management of Duchenne Muscular Dystrophy. Adv Pediatr 2020;67:183-196   Key points • Duchenne muscular dystrophy (DMD) is an X-linked, recessive, lethal disease characterized by progressive loss of muscle strength and function. Becker muscular dystrophy is less severe, although there is phenotypic overlap with DMD. • […]