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Wall A, Lee GH, Maldonado J, Magnus D. Genetic disease and intellectual disability as contraindications to transplant listing in the…

Naarding KJ, Doorenweerd N, Koeks Z, Hendriksen RGF, Chotkan KA, Krom YD, et al. Decision-Making And Selection Bias in Four…

Goemans N, Signorovitch J, Sajeev G, Yao Z, Gordish-Dressman H, McDonald CM, et al. Suitability of external controls for drug…

Sun C, Shen L, Zhang Z, Xie X. Therapeutic Strategies for Duchenne Muscular Dystrophy: An Update. Genes. 2020;11(8)   Abstract…

Łoboda A, Dulak J. Muscle and cardiac therapeutic strategies for Duchenne muscular dystrophy: past, present, and future. Pharmacol Rep 2020…

Babbs A, Chatzopoulou M, Edwards B, et al. From diagnosis to therapy in Duchenne muscular dystrophy. Biochem Soc Trans 2020…

Gieron-Korthals M, Fernandez R. New Developments in Diagnosis, Treatment, and Management of Duchenne Muscular Dystrophy. Adv Pediatr 2020;67:183-196   Key…

Kumar SH, Athimoolam K, Suraj M, et al. Comprehensive genetic analysis of 961 unrelated Duchenne Muscular Dystrophy patients: Focus on…

Datta N, Ghosh PS. Update on Muscular Dystrophies with Focus on Novel Treatments and Biomarkers. Curr Neurol Neurosci Rep 2020;20:14…

Fay AJ, Knox R, Neil EE, Strober J. Targeted Treatments for Inherited Neuromuscular Diseases of Childhood. Semin Neurol 2020;40:335-341  …