Library

Datta N, Ghosh PS. Update on Muscular Dystrophies with Focus on Novel Treatments and Biomarkers. Curr Neurol Neurosci Rep 2020;20:14…

Fay AJ, Knox R, Neil EE, Strober J. Targeted Treatments for Inherited Neuromuscular Diseases of Childhood. Semin Neurol 2020  …

Salmaninejad A, Jafari Abarghan Y, Bozorg Qomi S, et al. Common therapeutic advances for Duchenne muscular dystrophy (DMD). Int J…

Barnard AM, Riehl SL, Willcocks RJ, Walter GA, Angell AM, Vandenborne K. Characterizing Enrollment in Observational Studies of Duchenne Muscular…

Grages SM, Bell M, Berlau DJ. New and emerging pharmacotherapy for duchenne muscular dystrophy: a focus on synthetic therapeutics. Expert…

Crossnohere NL, Fischer R, Crossley E, Vroom E, Bridges JF. The evolution of patient-focused drug development and Duchenne muscular dystrophy.…

Angelini C, Marozzo R, Pegoraro V. Current and emerging therapies in Becker muscular dystrophy (BMD). Acta myologica : myopathies and…

Gogou M, Pavlou E, Haidopoulou K. Therapies that are available and under development for Duchenne muscular dystrophy: What about lung…

Thangarajh M. The Dystrophinopathies. Continuum (Minneapolis, Minn.) 2019;25:1619-1639   Abstract PURPOSE OF REVIEW: The dystrophinopathies are among the most common…

Mercuri E, Bonnemann CG, Muntoni F. Muscular dystrophies. Lancet (London, England) 2019;394:2025-2038   Abstract Muscular dystrophies are primary diseases of…