1 2 aim

Decision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy

Naarding KJ, Doorenweerd N, Koeks Z, Hendriksen RGF, Chotkan KA, Krom YD, et al. Decision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy. Journal of neuromuscular diseases. 2020;7:433-442   Abstract BACKGROUND: Natural history data are essential for trial design in Duchenne (DMD) and Becker muscular dystrophy (BMD), but recruitment for […]