The evolution of patient-focused drug development and Duchenne muscular dystrophy

Crossnohere NL, Fischer R, Crossley E, Vroom E, Bridges JF. The evolution of patient-focused drug development and Duchenne muscular dystrophy. Expert review of pharmacoeconomics & outcomes research 2020;20:57-68   Abstract Introduction: There is a groundswell of interest from patient, industry, and groups to rigorously and transparently integrate patient-voice into regulatory decision-making. Patient-focused drug development (PFDD) […]