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Heydemann A. Skeletal Muscle Metabolism in Duchenne and Becker Muscular Dystrophy-Implications for Therapies. Nutrients 2018;10   Abstract The interactions between…

Korinthenberg R. A new era in the management of Duchenne muscular dystrophy. Developmental medicine and child neurology 2019;61:292-297   Abstract The…

Franson T, Kinnett K, Cripe TP. Unique Burdens of Pediatric Clinical Trials in Duchenne Muscular Dystrophy, April 20-21, 2017, Bethesda,…

Cordova G, Negroni E, Cabello-Verrugio C, Mouly V, Trollet C. Combined Therapies for Duchenne Muscular Dystrophy to Optimize Treatment Efficacy.…

Ionita C, Kinnett K, Mathews K. Collective Statement Regarding Patient Access to Approved Therapies from the Center Directors of Parent…

Ricotti V, Muntoni F, Voit T. Challenges of clinical trial design for DMD. Neuromuscular disorders : NMD 2015;25:932-5 Including a…

Leigh F, Ferlini A, Biggar D, et al. Neurology Care, Diagnostics, and Emerging Therapies of the Patient With Duchenne Muscular…

Goemans N, Buyse G. Current treatment and management of dystrophinopathies. Current treatment options in neurology 2014;16:287.   Opinion statement •…

Scheuerbrandt G. First meeting of the Duchenne Parent Project in Europe: Treatment of Duchenne Muscular Dystrophy. 7-8 November 1997, Rotterdam,…

Wang RT, Nelson SF. What can Duchenne Connect teach us about treating Duchenne muscular dystrophy? Current opinion in neurology 2015;28:535-41.…