Current treatment and management of dystrophinopathies

Goemans N, Buyse G. Current treatment and management of dystrophinopathies. Current treatment options in neurology 2014;16:287.   Opinion statement • Duchenne muscular dystrophy (DMD), the most common and severe type of dystrophinopathy, is a progressive disease affecting primordially skeletal and cardiac muscle. A coordinated multidisciplinary approach is required to address its multisystemic manifestations and secondary […]