Library

Iannaccone ST, Hynan LS, Morton A, Buchanan R, Limbers CA, Varni JW. The PedsQL in pediatric patients with Spinal Muscular…

Klingels K, Mayhew AG, Mazzone ES, et al. Development of a patient-reported outcome measure for upper limb function in Duchenne…

Henricson E, Abresch R, Han JJ, et al. The 6-Minute Walk Test and Person-Reported Outcomes in Boys with Duchenne Muscular…

McDonald CM, Henricson EK, Abresch RT, et al. The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy:…

Messina S, Vita GL, Sframeli M, et al. Health-related quality of life and functional changes in DMD: A 12-month longitudinal…

Ricotti V, Selby V, Ridout D, et al. Respiratory and upper limb function as outcome measures in ambulant and non-ambulant…

Powell PA, Carlton J, Rowen D, Brazier JE. Producing a preference-based quality of life measure for people with Duchenne muscular…

Fayssoil A, Chaffaut C, Ogna A, et al. Echographic Assessment of Diaphragmatic Function in Duchenne Muscular Dystrophy from Childhood to…

Senesac CR, Lott DJ, Willcocks RJ, Duong T, Smith BK. Lower Extremity Functional Outcome Measures in Duchenne Muscular Dystrophy-A Delphi…

Aartsma-Rus A, Morgan J, Lonkar P, et al. Report of a TREAT-NMD/World Duchenne Organisation Meeting on Dystrophin Quantification Methodology. Journal…