Lower Extremity Functional Outcome Measures in Duchenne Muscular Dystrophy-A Delphi Survey
Senesac CR, Lott DJ, Willcocks RJ, Duong T, Smith BK. Lower Extremity Functional Outcome Measures in Duchenne Muscular Dystrophy-A Delphi Survey. Journal of neuromuscular diseases 2019;6:75-83 Abstract INTRODUCTION: Duchenne muscular dystrophy (DMD) is a neuromuscular disease caused by a dystrophin protein deficiency. dystrophin functions to stabilize and protect the muscle fiber during muscle contraction; […]