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McNally EM, Wyatt EJ. Mutation-Based Therapy for Duchenne Muscular Dystrophy: Antisense Treatment Arrives in the Clinic. Circulation 2017;136:979-981

Connolly AM, Zaidman CM, Golumbek PT, et al. Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy. Muscle…

Hughes MC, Ramos SV, Turnbull PC, et al. Impairments in left ventricular mitochondrial bioenergetics precede overt cardiac dysfunction and remodelling…

Nakamura A. Mutation-Based Therapeutic Strategies for Duchenne Muscular Dystrophy: From Genetic Diagnosis to Therapy. Journal of personalized medicine 2019;9  …

Ricotti V, Selby V, Ridout D, et al. Respiratory and upper limb function as outcome measures in ambulant and non-ambulant…

Powell PA, Carlton J, Rowen D, Brazier JE. Producing a preference-based quality of life measure for people with Duchenne muscular…

Wong SC, Straub V, Ward LM, Quinlivan R, th Ewp. 236th ENMC International Workshop Bone protective therapy in Duchenne muscular…

Scavone C, di Mauro G, Mascolo A, Berrino L, Rossi F, Capuano A. The New Paradigms in Clinical Research: From…

Zhong J, Xie Y, Bhandari V, et al. Clinical and genetic characteristics of female dystrophinopathy carriers. Mol Med Rep 2019;19:3035-3044…

Vorster N, Evans K, Murphy N, et al. Powered standing wheelchairs promote independence, health and community involvement in adolescents with…