A qualitative study of experiences of health and social care in home mechanical ventilation
MacLaren J, Smith P, Rodgers S, Bateman AP, Ramsay P. A qualitative study of experiences of health and social care…
Don't forget the trunk in Duchenne muscular dystrophy patients: more muscle weakness and compensation than expected
Peeters LHC, Kingma I, van Dieen JH, de Groot IJM. Don't forget the trunk in Duchenne muscular dystrophy patients: more…
Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy
Nelson CE, Wu Y, Gemberling MP, et al. Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy. Nature medicine…
Duchenne muscular dystrophy: Focus on arachidonic acid metabolites
Hoxha M. Duchenne muscular dystrophy: Focus on arachidonic acid metabolites. Biomedicine & pharmacotherapy = Biomedecine & pharmacotherapie 2019;110:796-802 Abstract…
Restoring Dystrophin Expression in Duchenne Muscular Dystrophy: Current Status of Therapeutic Approaches
Shimizu-Motohashi Y, Komaki H, Motohashi N, Takeda S, Yokota T, Aoki Y. Restoring Dystrophin Expression in Duchenne Muscular Dystrophy: Current…
Long-Term Ventilation in Neuromuscular Patients: Review of Concerns, Beliefs, and Ethical Dilemmas
Crimi C, Pierucci P, Carlucci A, Cortegiani A, Gregoretti C. Long-Term Ventilation in Neuromuscular Patients: Review of Concerns, Beliefs, and…
Screening and evaluation tools of dysphagia in adults with neuromuscular diseases: a systematic review
Audag N, Goubau C, Toussaint M, Reychler G. Screening and evaluation tools of dysphagia in adults with neuromuscular diseases: a…
Precision Medicine and Exercise Therapy in Duchenne Muscular Dystrophy
Kostek M. Precision Medicine and Exercise Therapy in Duchenne Muscular Dystrophy. Sports (Basel, Switzerland) 2019;7 Abstract Precision medicine is…
Age-dependent changes in metabolite profile and lipid saturation in dystrophic mice
Lee-McMullen B, Chrzanowski SM, Vohra R, et al. Age-dependent changes in metabolite profile and lipid saturation in dystrophic mice. NMR…
Fractures and Linear Growth in a Nationwide Cohort of Boys With Duchenne Muscular Dystrophy With and Without Glucocorticoid Treatment: Results From the UK NorthStar Database
Joseph S, Wang C, Bushby K, et al. Fractures and Linear Growth in a Nationwide Cohort of Boys With Duchenne…
