Genotype and age at diagnosis in Thai boys with Duchenne muscular dystrophy (DMD)
Yamputchong P, Pho-Iam T, Limwongse C, Wattanasirichaigoon D, Sanmaneechai O. Genotype and age at diagnosis in Thai boys with Duchenne…
Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides
Nordin JZ, Mizobe Y, Nakamura H, Komaki H, Takeda S, Aoki Y. Characterizing Exon Skipping Efficiency in DMD Patient Samples…
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Smith EC, Conklin LS, Hoffman EP, Clemens PR, Mah JK, Finkel RS, et al. Efficacy and safety of vamorolone in…
Decision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy
Naarding KJ, Doorenweerd N, Koeks Z, Hendriksen RGF, Chotkan KA, Krom YD, et al. Decision-Making And Selection Bias in Four…
Genetic testing offer for inherited neuromuscular diseases within the EURO-NMD reference network: A European survey study
Peterlin B, Gualandi F, Maver A, Servidei S, van der Maarel SM, Lamy F, et al. Genetic testing offer for…
Longitudinal Evaluation of Working Memory in Duchenne Muscular Dystrophy
Thangarajh M, Elfring GL, Trifillis P. Longitudinal Evaluation of Working Memory in Duchenne Muscular Dystrophy. Journal of clinical medicine. 2020;9(9)…
Advances in Genetic Characterization and Genotype-Phenotype Correlation of Duchenne and Becker Muscular Dystrophy in the Personalized Medicine Era
Sheikh O, Yokota T. Advances in Genetic Characterization and Genotype-Phenotype Correlation of Duchenne and Becker Muscular Dystrophy in the Personalized…
Exploring physiological signals on people with Duchenne muscular dystrophy for an active trunk support: a case study
Verros S, Peeters L, Bergsma A, Hekman EEG, Verkerke GJ, Koopman B. Exploring physiological signals on people with Duchenne muscular…
Evaluation of Admittance Control as an Alternative to Passive Arm Supports to Increase Upper Extremity Function for Individuals with Duchenne Muscular Dystrophy
Corrigan MC, Foulds RA. Evaluation of admittance control as an alternative to passive arm supports to increase upper extremity function…
Suitability of external controls for drug evaluation in Duchenne muscular dystrophy
Goemans N, Signorovitch J, Sajeev G, Yao Z, Gordish-Dressman H, McDonald CM, et al. Suitability of external controls for drug…
