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McDonald CM, Henricson EK, Abresch RT, et al. Long-term effects of glucocorticoids on function, quality of life, and survival in…

McDonald CM, Sajeev G, Yao Z, et al. Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta-analysis of disease…

Koeks Z, Bladen CL, Salgado D, et al. Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from…

Merlini L, Gennari M, Malaspina E, et al. Early corticosteroid treatment in 4 Duchenne muscular dystrophy patients: 14-year follow-up. Muscle…

Sertpoyraz FM, Tiftikcioglu BI. The relationship of bone mineral density and vitamin D levels with steroid use and ambulation in…

Hoffman EP, Schwartz BD, Mengle-Gaw LJ, et al. Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function.…

Cowen L, Mancini M, Martin A, Lucas A, Donovan JM. Variability and trends in corticosteroid use by male United States…

Henricson EK, Abresch RT, Cnaan A, et al. The cooperative international neuromuscular research group Duchenne natural history study: glucocorticoid treatment…

Vamorolone (VBP15): a steroid-alternative Trial publications Phase I single ascending dose study VBP15-001 (NCT02415439) A Phase 1 Single Ascending Dose and…

Wong BL, Rybalsky I, Shellenbarger KC, et al. Long-Term Outcome of Interdisciplinary Management of Patients with Duchenne Muscular Dystrophy Receiving…