Library

Li X, Conklin LS, van den Anker J, Hoffman EP, Clemens PR, Jusko WJ. Exposure-Response Analysis of Vamorolone (VBP15) in…

Wood CL, Cheetham TD, Guglieri M, et al. Testosterone Treatment of Pubertal Delay in Duchenne Muscular Dystrophy. Neuropediatrics 2015;46:371-6  …

Annexstad EJ, Bollerslev J, Westvik J, et al. The role of delayed bone age in the evaluation of stature and…

Gogou M, Pavlou E, Haidopoulou K. Therapies that are available and under development for Duchenne muscular dystrophy: What about lung…

Angliss ME, Sclip KD, Gauld L. Early NIV is associated with accelerated lung function decline in Duchenne muscular dystrophy treated…

Hoffman EP, Riddle V, Siegler MA, et al. Phase 1 trial of vamorolone, a first-in-class steroid, shows improvements in side…

Bylo M, Farewell R, Coppenrath VA, Yogaratnam D. A Review of Deflazacort for Patients With Duchenne Muscular Dystrophy. Ann Pharmacother…

Takeuchi F, Nakamura H, Yonemoto N, et al. Clinical practice with steroid therapy for Duchenne muscular dystrophy: An expert survey…

Kinnett K, Noritz G. The PJ Nicholoff Steroid Protocol for Duchenne and Becker Muscular Dystrophy and Adrenal Suppression. PLoS currents…

Marden JR, Freimark J, Yao Z, Signorovitch J, Tian C, Wong BL. Real-world outcomes of long-term prednisone and deflazacort use…