Novel compounds for the treatment of Duchenne muscular dystrophy: emerging therapeutic agents

Wilton SD, Fletcher S. Novel compounds for the treatment of Duchenne muscular dystrophy: emerging therapeutic agents. The application of clinical genetics 2011;4:29-44   Abstract The identification of dystrophin and the causative role of mutations in this gene in Duchenne and Becker muscular dystrophies (D/BMD) was expected to lead to timely development of effective therapies. Despite […]