Online Self-Report Data for Duchenne Muscular Dystrophy Confirms Natural History and Can Be Used to Assess for Therapeutic Benefits

Wang RT, Silverstein Fadlon CA, Ulm JW, et al. Online self-report data for duchenne muscular dystrophy confirms natural history and can be used to assess for therapeutic benefits. PLoS currents 2014;6.   Abstract To assess the utility of online patient self-report outcomes in a rare disease, we attempted to observe the effects of corticosteroids in […]