1 2 aim

Utrophin upregulation by ezutromid (SMT C1100) [terminated]

Ricotti V, Spinty S, Roper H, et al. Safety, Tolerability, and Pharmacokinetics of SMT C1100, a 2-Arylbenzoxazole Utrophin Modulator, following Single- and Multiple-Dose Administration to Pediatric Patients with Duchenne Muscular Dystrophy. PloS one 2016;11:e0152840 Muntoni F, Tejura B, Spinty S, et al. A Phase 1b Trial to Assess the Pharmacokinetics of Ezutromid in Pediatric Duchenne […]