The effect of emerging molecular and genetic therapies on cardiopulmonary disease in Duchenne muscular dystrophy

McKim DA, Cripe TP, Cripe LH. The effect of emerging molecular and genetic therapies on cardiopulmonary disease in Duchenne muscular dystrophy. Pediatr Pulm 2020   Abstract Gene therapy is an attractive approach being intensively studied to prevent muscle deterioration in patients with Duchenne muscular dystrophy. While clinical trials are only in early stages, initial reports […]