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The development of CRISPR-mediated systems in the study of Duchenne muscular dystrophy

Cai A, Kong X. Development of CRISPR-Mediated Systems in the Study of Duchenne Muscular Dystrophy. Human gene therapy methods 2019;30:71-80   Abstract Duchenne muscular dystrophy (DMD) is a severe type of X-linked recessive degenerative muscle disease, caused by mutations in the dystrophin (DMD) gene on the X chromosome. The DMD gene is complex, consisting of […]