Prognostic factors for changes in the timed 4-stair climb in patients with Duchenne muscular dystrophy, and implications for measuring drug efficacy: A multi-institutional collaboration

Goemans N, Wong B, Van den Hauwe M, et al. Prognostic factors for changes in the timed 4-stair climb in patients with Duchenne muscular dystrophy, and implications for measuring drug efficacy: A multi-institutional collaboration. Plos One 2020;15:e0232870   Abstract PMC7302444 from Astellas Pharma (Mitobridge), Catabasis, FibroGen Inc., Italfarmaco SpA, Pfizer Inc., PTC Therapeutics, Roche, Sarepta […]