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Overview of drisapersen (GSK2402968/PRO051) clinical trials

Development (and thereby all open-label extension studies) has been terminated Trial publications Exploratory study on the local dystrophin production restoring effect and safety and tolerability of a single intramuscular dose of antisense oligoribonucleotide PRO051 in Duchenne muscular dystrophy patients Phase I local treatment (NL651/NTR712) • van Deutekom JC, Janson AA, Ginjaar IB, et al. Local dystrophin […]