Clinical Investigation of Duchenne Muscular Dystrophy

Mendell JR, Province MA, Moxley RT, 3rd, et al. Clinical investigation of Duchenne muscular dystrophy. A methodology for therapeutic trials based on natural history controls. Archives of neurology 1987;44:808-11   Abstract Between 1979 and 1987 we documented the natural history of Duchenne muscular dystrophy in 170 patients, aged from 3 to 23 years, by making […]