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Life-Long AAV-Mediated CRISPR Genome Editing in Dystrophic Heart Improves Cardiomyopathy without Causing Serious Lesions in mdx Mice

Xu L, Lau YS, Gao Y, Li H, Han R. Life-Long AAV-Mediated CRISPR Genome Editing in Dystrophic Heart Improves Cardiomyopathy without Causing Serious Lesions in mdx Mice. Molecular therapy : the journal of the American Society of Gene Therapy 2019;27:1407-1414   Abstract Previous studies from others and us have demonstrated that CRISPR genome editing could […]