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Gene specific therapies – the next therapeutic milestone in neurology

Brenner D, Ludolph AC, Weishaupt JH. Gene specific therapies – the next therapeutic milestone in neurology. Neurol Res Pract 2020;2:25   Abstract Gene selective approaches that either correct a disease mutation or a pathogenic mechanism will fundamentally change the treatment of neurological disorders. Basically, gene specific therapies are designed to manipulate RNA expression or reconstitute […]