Cardiopulmonary phenotypic variability and discordance in Duchenne muscular dystrophy: implications for new therapies

Birnkrant DJ, Carter JC. Cardiopulmonary phenotypic variability and discordance in Duchenne muscular dystrophy: implications for new therapies. Pediatr Pulm 2020   Abstract Neuromuscular respiratory medicine has traditionally focused on assisted lung ventilation and mucus clearance. These therapies have prolonged survival for patients with Duchenne muscular dystrophy (DMD). However, the field is rapidly evolving in a […]