ENMC workshops on Biomarkers and surrogate endpoints in Duchenne

Several workshops have been held concerning the possibilities of using biomarkers as surrogate endpoints in therapy development for DMD.   Explanation on biomarkers Aartsma-Rus A, Ferlini A, Vroom E. Biomarkers and surrogate endpoints in Duchenne: meeting report. Neuromuscular disorders : NMD 2014;24:743-5   Workshop reports of two workshops in 2014 resp. 2017 Ferlini A, Flanigan […]