Assessment of Treatment Effect With Multiple Outcomes in 2 Clinical Trials of Patients With Duchenne Muscular Dystrophy

Li D, McDonald CM, Elfring GL, et al. Assessment of Treatment Effect With Multiple Outcomes in 2 Clinical Trials of Patients With Duchenne Muscular Dystrophy. JAMA network open 2020;3:e1921306   Introduction Clinical studies routinely collect data on multiple efficacy or safety end points. Conventionally, summaries for the treatment effect are presented for each end point […]