Library

Panovsky R, Pesl M, Holecek T, et al. Cardiac profile of the Czech population of Duchenne muscular dystrophy patients: a…

Kong R, Laskin OL, Kaushik D, et al. Ataluren Pharmacokinetics in Healthy Japanese and Caucasian Subjects. Clinical pharmacology in drug…

Soslow JH, Damon BM, Saville BR, et al. Evaluation of post-contrast myocardial t1 in duchenne muscular dystrophy using cardiac magnetic…

Duan D. Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy. Molecular therapy : the journal of the American Society…

Propp R, McAdam L, Davis AM, et al. Development and content validation of the Muscular Dystrophy Child Health Index of…

Hor KN, Mah ML, Johnston P, Cripe TP, Cripe LH. Advances in the diagnosis and management of cardiomyopathy in Duchenne…

Straub V, Mercuri E, group DMDoms. Report on the workshop: Meaningful outcome measures for Duchenne muscular dystrophy, London, UK, 30-31…

Shieh PB, McIntosh J, Jin F, et al. Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation:…

Verhaart IEC, van den Engel-Hoek L, Fiorotto ML, Franken-Verbeek M, Vroom E, workshop p. Nutrition in Duchenne muscular dystrophy 16-18…

Pane M, Coratti G, Brogna C, et al. Upper limb function in Duchenne muscular dystrophy: 24 month longitudinal data. PloS…