Home-Based Monitoring of Pulmonary Function in Patients with Duchenne Muscular Dystrophy
Buyse GM, Rummey C, Meier T, et al. Home-Based Monitoring of Pulmonary Function in Patients with Duchenne Muscular Dystrophy. Journal…
Health Care Transition Experiences of Males with Childhood-onset Duchenne and Becker Muscular Dystrophy: Findings from the Muscular Dystrophy Surveillance Tracking and Research Network (MD STARnet) Health Care Transitions and Other Life Experiences Survey
Paramsothy P PhD MPH, Herron Ar PhD MA, Lamb MMP, et al. Health Care Transition Experiences of Males with Childhood-onset…
Clinical management of Duchenne muscular dystrophy: the state of the art
Messina S, Vita GL. Clinical management of Duchenne muscular dystrophy: the state of the art. Neurological sciences : official journal…
Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug
Conklin LS, Damsker JM, Hoffman EP, et al. Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class…
Timed function tests have withstood the test of time as clinically meaningful and responsive endpoints in duchenne muscular dystrophy
McDonald CM. Timed function tests have withstood the test of time as clinically meaningful and responsive endpoints in duchenne muscular…
A mini-review and implementation model for using ataluren to treat nonsense mutation Duchenne muscular dystrophy
Landfeldt E, Sejersen T, Tulinius M. A mini-review and implementation model for using ataluren to treat nonsense mutation Duchenne muscular…
Body composition and body mass index in Duchenne dystrophy: Role of dietary intake
Bernabe-Garcia M, Rodriguez-Cruz M, Atilano S, et al. Body composition and body mass index in Duchenne muscular dystrophy: Role of…
Bone Health and Endocrine Care of Boys with Duchenne Muscular Dystrophy: Data from the MD STARnet
Weber DR, Thomas S, Erickson SW, et al. Bone Health and Endocrine Care of Boys with Duchenne Muscular Dystrophy: Data…
Sleep disordered breathing in Duchenne muscular dystrophy
Sawnani H. Sleep disordered breathing in Duchenne muscular dystrophy. Paediatric respiratory reviews 2019;30:2-8 Abstract Symptoms of sleep disordered breathing…
Placebo-controlled Phase 2 Trial of Drisapersen for Duchenne Muscular Dystrophy
McDonald CM, Wong B, Flanigan KM, et al. Placebo-controlled Phase 2 Trial of Drisapersen for Duchenne Muscular Dystrophy. Annals of…
