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McDonald CM, Henricson EK, Abresch RT, et al. The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy:…

Messina S, Vita GL, Sframeli M, et al. Health-related quality of life and functional changes in DMD: A 12-month longitudinal…

Vamorolone (VBP15): a steroid-alternative Trial publications Phase I single ascending dose study VBP15-001 (NCT02415439) A Phase 1 Single Ascending Dose and…

Bann CM, Abresch RT, Biesecker B, et al. Measuring quality of life in muscular dystrophy. Neurology 2015;84:1034-42   Abstract OBJECTIVES:…

Hong Y, Wang Y, Zhang Y, et al. Risk factors for falls among boys under 18 years with muscular dystrophy.…

Vermeulen KM, Lopes M, Grilo EC, Alves CX, Machado RJA, Lais LL, et al. Bioelectrical impedance vector analysis and phase…

Verhaart IEC, van de Vijver D, Boertje-van der Meulen JW, Putker K, Adamzek K, Aartsma-Rus A, et al. A modified…

Wood CL, Cheetham TD, Hollingsworth KG, Guglieri M, Ailins-Sahun Y, Punniyakodi S, et al. Observational study of clinical outcomes for…

Janssen M, Harlaar J, Koopman B, de Groot IJM. Unraveling upper extremity performance in Duchenne muscular dystrophy: A biophysical model.…

Ma KM, Thomas ES, Wereszczynski J, Menhart N. Empirical and Computational Comparison of Alternative Therapeutic Exon Skip Repairs for Duchenne…