Library

He WB, Du J, Xie PY, et al. X-chromosome inactivation pattern of amniocytes predicts the risk of dystrophinopathy in fetal…

Dittrich S, Graf E, Trollmann R, et al. Effect and safety of treatment with ACE-inhibitor Enalapril and beta-blocker metoprolol on…

Finder J, Mayer OH, Sheehan D, et al. Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary. American journal of…

Le Moing AG, Seferian AM, Moraux A, et al. A Movement Monitor Based on Magneto-Inertial Sensors for Non-Ambulant Patients with…

Trial publications Phase IIa placebo controlled study (NCT00654784) and open label extension study (NCT00758225) Efficacy and Tolerability of Idebenone in…

Meier T, Rummey C, Leinonen M, Spagnolo P, Mayer OH, Buyse GM. Characterization of pulmonary function in 10-18 year old…

Landrum Peay H, Fischer R, Tzeng JP, et al. Gene therapy as a potential therapeutic option for Duchenne muscular dystrophy:…

Cowen L, Mancini M, Martin A, Lucas A, Donovan JM. Variability and trends in corticosteroid use by male United States…

Thongsing A, Likasitwattanakul S, Sanmaneechai O. Reliability and validity of the Thai version of the Pediatric Quality of Life inventory…

Balasubramanian G, Morampudi S, Chhabra P, Gowda A, Zomorodi B. An overview of Compassionate Use Programs in the European Union…