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Pascual Morena C, Martinez-Vizcaino V, Alvarez-Bueno C, et al. Effectiveness of pharmacological treatments in Duchenne muscular dystrophy: a protocol for…

Pascoe JE, Sawnani H, Hater B, Sketch M, Modi AC. Understanding adherence to noninvasive ventilation in youth with Duchenne muscular…

Muntoni F, Domingos J, Manzur AY, et al. Categorising trajectories and individual item changes of the North Star Ambulatory Assessment…

Silva IS, Pedrosa R, Azevedo IG, et al. Respiratory muscle training in children and adults with neuromuscular disease. Cochrane Db…

Annexstad EJ, Fagerheim T, Holm I, Rasmussen M. Molecular and Clinical Characteristics of a National Cohort of Paediatric Duchenne Muscular…

Fleck D, Curry C, Donnan K, et al. Investigating the clinical use of structured light plethysmography to assess lung function…

Lester G, Femia G, Ayer J, Puranik R. A case report: X-linked dystrophin gene mutation causing severe isolated dilated cardiomyopathy.…

Hoffman EP, Schwartz BD, Mengle-Gaw LJ, et al. Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function.…

Yang Y, He P, Li DZ. Germline mosaicism in a DMD family: incidental identification in prenatal diagnosis. Journal of obstetrics…

Thangarajh M, Kaat AJ, Bibat G, et al. The NIH Toolbox for cognitive surveillance in Duchenne muscular dystrophy. Annals of…