Development of the healthy pathways child-report scales
Bevans KB, Riley AW, Forrest CB. Development of the healthy pathways child-report scales. Quality of life research : an international…
Conceptual and methodological advances in child-reported outcomes measurement
Bevans KB, Riley AW, Moon J, Forrest CB. Conceptual and methodological advances in child-reported outcomes measurement. Expert review of pharmacoeconomics…
Longitudinal reliability of outcome measures in patients with Duchenne muscular dystrophy
Nagy S, Schadelin S, Hafner P, et al. Longitudinal reliability of outcome measures in patients with Duchenne muscular dystrophy. Muscle…
Toward a hybrid brain-machine interface for palliating motor handicap with Duchenne muscular dystrophy: a case report
Dupres A, Cabestaing F, Rouillard J, Tiffreau V, Pradeau C. Toward a hybrid brain-machine interface for palliating motor handicap with…
Recent advancements in exon-skipping therapies using antisense oligonucleotides and genome editing for the treatment of various muscular dystrophies
Hwang J, Yokota T. Recent advancements in exon-skipping therapies using antisense oligonucleotides and genome editing for the treatment of various…
Psychosocial adjustment and parental stress in Duchenne Muscular Dystrophy
Gocheva V, Schmidt S, Orsini AL, et al. Psychosocial adjustment and parental stress in Duchenne Muscular Dystrophy. European journal of…
Stabilization of Early Duchenne Cardiomyopathy With Aldosterone Inhibition: Results of the Multicenter AIDMD Trial
Raman SV, Hor KN, Mazur W, et al. Stabilization of Early Duchenne Cardiomyopathy With Aldosterone Inhibition: Results of the Multicenter…
Practical Considerations in Using Online Modified-Delphi Approaches to Engage Patients and Other Stakeholders in Clinical Practice Guideline Development
Khodyakov D, Grant S, Denger B, et al. Practical Considerations in Using Online Modified-Delphi Approaches to Engage Patients and Other…
Meeting on data sharing for Duchenne 21-22 March 2019 Amsterdam, the Netherlands
Verhaart IEC, ‘t Hoen PAC, Roos M, Vroom E. Meeting on data sharing for Duchenne 21–22 March 2019 Amsterdam, the…
Duchenne muscular dystrophy: an historical treatment review
Werneck LC, Lorenzoni PJ, Ducci RD, Fustes OH, Kay CSK, Scola RH. Duchenne muscular dystrophy: an historical treatment review. Arq…
