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Fujino H, Matsumura T, Saito T, Fujimura H, Imura O. Psychological Case Conference Following the Death of a Patient With…

Komaki H, Takeshima Y, Matsumura T, et al. Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study. Annals…

Kim HG, Eun LY, Park HK. Is It Possible for Children in Duchenne Muscular Dystrophy to Preserve Cardiac Function with…

Uechi L, Jalali M, Wilbur JD, et al. Complex genetic dependencies among growth and neurological phenotypes in healthy children: Towards…

Buscara L, Gross DA, Daniele N. Of rAAV and Men: From Genetic Neuromuscular Disorder Efficacy and Toxicity Preclinical Studies to…

Kincl V, Panovský R, Pešl M, et al. Echocardiographic signs of subclinical cardiac function impairment in Duchenne dystrophy gene carriers.…

Hayes EA, Nandi D. Is there a future for the use of left ventricular assist devices in Duchenne muscular dystrophy?…

Lim KRQ, Nguyen Q, Yokota T. Genotype-Phenotype Correlations in Duchenne and Becker Muscular Dystrophy Patients from the Canadian Neuromuscular Disease…

Sharma G, Sharma AR, Bhattacharya M, Lee SS, Chakraborty C. CRISPR-Cas9: A Preclinical and Clinical Perspective for the Treatment of…

de Feraudy Y, Yaou RB, Wahbi K, et al. Very low residual dystrophin quantity is associated with milder dystrophinopathy. Annals…