CRISPR Correction of Duchenne Muscular Dystrophy
Min YL, Bassel-Duby R, Olson EN. CRISPR Correction of Duchenne Muscular Dystrophy. Annual review of medicine 2019;70:239-255 Abstract The…
Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5(ch) and AAV1
Majowicz A, Salas D, Zabaleta N, et al. Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by…
Applications of CRISPR/Cas9 for the Treatment of Duchenne Muscular Dystrophy
Lim KRQ, Yoon C, Yokota T. Applications of CRISPR/Cas9 for the Treatment of Duchenne Muscular Dystrophy. Journal of personalized medicine…
AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice
Hakim CH, Wasala NB, Nelson CE, et al. AAV CRISPR editing rescues cardiac and muscle function for 18 months in…
Personalized gene and cell therapy for Duchenne Muscular Dystrophy
Barthelemy F, Wein N. Personalized gene and cell therapy for Duchenne Muscular Dystrophy. Neuromuscular disorders : NMD 2018;28:803-824 Abstract…
