Current Genetic Survey and Potential Gene-Targeting Therapeutics for Neuromuscular Diseases

Chiu W, Hsun YH, Chang KJ, et al. Current Genetic Survey and Potential Gene-Targeting Therapeutics for Neuromuscular Diseases. International journal of molecular sciences 2020;21   Abstract Neuromuscular diseases (NMDs) belong to a class of functional impairments that cause dysfunctions of the motor neuron-muscle functional axis components. Inherited monogenic neuromuscular disorders encompass both muscular dystrophies and […]