A Sequel to the Eteplirsen Saga: Eteplirsen Is Approved in the United States but Was Not Approved in Europe
Aartsma-Rus A, Goemans N. A Sequel to the Eteplirsen Saga: Eteplirsen Is Approved in the United States but Was Not…
Induced Pluripotent Stem Cells for Duchenne Muscular Dystrophy Modeling and Therapy
Danisovic L, Culenova M, Csobonyeiova M. Induced Pluripotent Stem Cells for Duchenne Muscular Dystrophy Modeling and Therapy. Cells 2018;7 …
Cough and airway clearance in Duchenne muscular dystrophy
Camela F, Gallucci M, Ricci G. Cough and airway clearance in Duchenne muscular dystrophy. Paediatric respiratory reviews 2019;31:35-39 Abstract People…
Growing patients with Duchenne muscular dystrophy: longitudinal changes in their dentofacial morphology and orofacial functional capacities
Fabienne Egli, Sébastien Botteron, Catherine Morel and Stavros Kiliaridis. Division of Orthodontics, School of Dentistry, University of Geneva, Switzerland Summary…
Growth, pubertal development, and skeletal health in boys with Duchenne Muscular Dystrophy
Ward LM, Weber DR. Growth, pubertal development, and skeletal health in boys with Duchenne Muscular Dystrophy. Current opinion in endocrinology,…
An Introduction to the Duchenne Muscular Dystrophy Care Considerations
Additonal information on the 2018 updated Care considerations In 2010, Bushby et al published the first-ever international comprehensive guidance on…
Neurology Care, Diagnostics, and Emerging Therapies of the Patient With Duchenne Muscular Dystrophy
Leigh F, Ferlini A, Biggar D, et al. Neurology Care, Diagnostics, and Emerging Therapies of the Patient With Duchenne Muscular…
Rehabilitation Management of the Patient With Duchenne Muscular Dystrophy
Case LE, Apkon SD, Eagle M, et al. Rehabilitation Management of the Patient With Duchenne Muscular Dystrophy. Pediatrics 2018;142:S17-s33 …
Bone Health and Osteoporosis Management of the Patient With Duchenne Muscular Dystrophy
Ward LM, Hadjiyannakis S, McMillan HJ, Noritz G, Weber DR. Bone Health and Osteoporosis Management of the Patient With Duchenne…
Nutritional and Gastrointestinal Management of the Patient With Duchenne Muscular Dystrophy
Brumbaugh D, Watne L, Gottrand F, et al. Nutritional and Gastrointestinal Management of the Patient With Duchenne Muscular Dystrophy. Pediatrics…
