The PJ Nicholoff Steroid Protocol for Duchenne and Becker Muscular Dystrophy and Adrenal Suppression
Kinnett K, Noritz G. The PJ Nicholoff Steroid Protocol for Duchenne and Becker Muscular Dystrophy and Adrenal Suppression. PLoS currents…
Improvements in health status and utility associated with ataluren for the treatment of nonsense mutation Duchenne muscular dystrophy
Landfeldt E, Lindberg C, Sejersen T. Improvements in health status and utility associated with ataluren for the treatment of nonsense…
Neurodevelopmental, behavioral, and emotional symptoms in Becker muscular dystrophy
Lambert JT, Darmahkasih AJ, Horn PS, et al. Neurodevelopmental, behavioral, and emotional symptoms in Becker muscular dystrophy. Muscle & nerve…
Caregiver preferences for emerging duchenne muscular dystrophy treatments: a comparison of best-worst scaling and conjoint analysis
Hollin IL, Peay HL, Bridges JF. Caregiver preferences for emerging duchenne muscular dystrophy treatments: a comparison of best-worst scaling and…
When Adolescent and Parents Disagree on Medical Plan, Who Gets to Decide?
Hopkins KA, Ott MA, Salih Z, Bosslet GT, Lantos J. When Adolescent and Parents Disagree on Medical Plan, Who Gets…
Monitoring daily physical activity of upper extremity in boys with Duchenne Muscular Dystrophy: A Pilot study
van der Geest A, Essers JMN, Bergsma A, Jansen M, de Groot IJM. Monitoring daily physical activity of upper extremity…
Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy: experience at a single, large care center
Marden JR, Freimark J, Yao Z, Signorovitch J, Tian C, Wong BL. Real-world outcomes of long-term prednisone and deflazacort use…
Diagnostic differences in respiratory breathing patterns and work of breathing indices in children with Duchenne muscular dystrophy
Ryan L, Rahman T, Strang A, Heinle R, Shaffer TH. Diagnostic differences in respiratory breathing patterns and work of breathing…
Tamoxifen in Duchenne muscular dystrophy (TAMDMD): study protocol for a multicenter, randomized, placebo-controlled, double-blind phase 3 trial
Nagy S, Hafner P, Schmidt S, et al. Tamoxifen in Duchenne muscular dystrophy (TAMDMD): study protocol for a multicenter, randomized,…
Becker muscular dystrophy caused by exon 2-truncating mutation of DMD.
Ikeda T, Fujinaka H, Goto K, Nakajima T, Ozawa T. Becker muscular dystrophy caused by exon 2-truncating mutation of DMD.…
