Library

Kinane TB, Mayer OH, Duda PW, Lowes LP, Moody SL, Mendell JR. Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison…

Cirak S, Arechavala-Gomeza V, Guglieri M, et al. Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after…

Cirak S, Feng L, Anthony K, et al. Restoration of the dystrophin-associated glycoprotein complex after exon skipping therapy in Duchenne…

Kinali M, Arechavala-Gomeza V, Feng L, et al. Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne…

Bylo M, Farewell R, Coppenrath VA, Yogaratnam D. A Review of Deflazacort for Patients With Duchenne Muscular Dystrophy. Ann Pharmacother…

Segawa K, Sugawara N, Maruo K, et al. Left Ventricular End-Diastolic Diameter and Cardiac Mortality in Duchenne Muscular Dystrophy. Neuropsych…

Silva THD, Anequini IP, Favero FM, et al. Functional performance and muscular strength in symptomatic female carriers of Duchenne muscular…

Ropars J, Gravot F, Ben Salem D, Rousseau F, Brochard S, Pons C. Muscle MRI: A biomarker of disease severity…

Heo YA. Golodirsen: First Approval. Drugs 2020;80:329-333   Abstract Golodirsen (Vyondys 53), an antisense oligonucleotide of the phophorodiamidate morpholino oligomer…

Wittlieb-Weber CA, Knecht KR, Villa CR, et al. Risk Factors for Cardiac and Non-cardiac Causes of Death in Males with…