Library

Haas M, Vlcek V, Balabanov P, et al. European Medicines Agency review of ataluren for the treatment of ambulant patients…

Bushby K, Finkel R, Wong B, et al. Ataluren treatment of patients with nonsense mutation dystrophinopathy. Muscle & nerve 2014;50:477-87…

Finkel RS, Flanigan KM, Wong B, et al. Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation…

Vicari S, Piccini G, Mercuri E, et al. Implicit learning deficit in children with Duchenne muscular dystrophy: Evidence for a…

Latimer R, Street N, Conway KC, et al. Secondary Conditions Among Males With Duchenne or Becker Muscular Dystrophy. J Child…

Hendriksen RGF, Vles JSH, Aalbers MW, Chin RFM, Hendriksen JGM. Brain-related comorbidities in boys and men with Duchenne Muscular Dystrophy:…

Darmahkasih AJ, Rybalsky I, Tian C, et al. Neurodevelopmental, behavioral, and emotional symptoms common in Duchenne muscular dystrophy. Muscle &…

Mayer OH, Leinonen M, Rummey C, Meier T, Buyse GM, Group DS. Efficacy of Idebenone to Preserve Respiratory Function above Clinically…

Buyse GM, Voit T, Schara U, et al. Treatment effect of idebenone on inspiratory function in patients with Duchenne muscular…

McDonald CM, Meier T, Voit T, et al. Idebenone reduces respiratory complications in patients with Duchenne muscular dystrophy. Neuromuscular disorders…