Exploring preclinical and clinical studies that might not have met expectation

The World Duchenne Organization is happy to hear that Duchenne Parent Project NL and Parent Project MD are supporting the Duchenne-specific submissions to the Journal of Neuromuscular Diseases exploring preclinical and clinical studies that might not have met expectation.

Both organizations have been funding and promoting research towards a cure for more than 25 years. We promote ‘learning from each other’ and avoiding duplications in research. The Journal of Neuromuscular Diseases, in a special issue led by Dr. Annemieke Aartsma-Rus and dr Virginia Archevala-Gomeza, has put out a call to analyze well-done research and trials which didn’t reach their predicted outcome so that we can learn from the past to improve research and trials today and look towards the future.

“The Null Hypothesis Stands” is new section in JND dedicated to well-done studies where results do not support the intervention tested and yet in doing so generate very useful data for the field. They are seeking contributions for a special issue on this topic.

Read the “Call for Papers” here (submission deadline: March 2021)

Learning from these ‘Negative Results’ will help avoid unnecessary testing in humans and animals, as well as save money and our most precious resource, time, as we continue the fight to end Duchenne.